Clinical Research

Clinical Research Resources

Clinical Research

Clinical research studies, also called clinical trials, are how doctors learn if an investigational medicine is safe and can be used to treat a disease and improve the health of people.

Clinical research studies, or clinical trials, are conducted to:

    • Determine if a new medicine is safe and identify side effects;
    • Study the effects of a new medicine and determine if it is effective in treating a disease;
    • Provide critical information needed to submit new medicines to government agencies that determine if medicines can be prescribed to treat a disease; and
    • Gather scientific evidence that has the potential to inform future patient care.

Choosing to participate in clinical research is a personal and individual decision. The following factors are common motivations for participants:

Access an investigational medication

Learn more about their disease

Help advance science

Potentially help save or improve lives of other patients in the future

There are benefits and risks to participating in a clinical research study. As part of the informed consent process, the study doctor and team will review with you the benefits and risks of joining the ELEVATE 1 clinical study.

Clinical Research Resources

    • Toolkit for patients with rare diseases to learn more about clinical research.

References

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